• Activating Nrf2 Protein Might Prevent Nerve Cell Degeneration in Friedreich’s Ataxia, Study Finds
  • Early Targeting of Mitochondrial Dysfunction May Help FA Patients, Study Suggests
  • Biomarin Advances Compound for Human Friedreich’s Ataxia Trials
  • Transplanting HSPCs Restored Mitochondria Function in FA Mice Model
  • European Medicines Agency Approves Orphan Product Designation as Potential Gene Therapy for FA
  • Children’s National, NORD Partner to Create Rare Disease ‘Centers of Excellence’
  • Engineered Frataxin Protein Improves Lifespan of Mice with Friedreich’s Ataxia, Study Shows
  • Sorting out Your Relationships
  • Pakistani Friedreich’s Ataxia Patient Forms Nonprofit to Raise Local Awareness of FA
  • Reata Enrolls First FA Patient in Part 2 of MOXIe Trial Evaluating Omaveloxolone Treatment
  • Dishing Up Anxiety
  • #NORDsummit – Alternatives to Large Placebo Trials, Grant Awards Among Ways FDA Supporting Rare Diseases, Chief Says