Graviton Bioscience has launched a Phase 2 clinical trial to test its experimental therapy GV101 in people with Friedreich’s ataxia (FA). The trial (NCT07870590) is planned to enroll 48 people with FA, ages 16 to 40, who are able to walk (with or without assistance) and who…
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I don’t think I will ever get used to having workmen in my house. The kitchen renovation continues, and the other morning, the workers gave me a story I think those of you in the Friedreich’s ataxia (FA) community can relate to. The carpenters told me they’d be at…
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A first-in-human trial testing Adjuvia Therapeutics‘ ATI-105 for Friedreich’s ataxia (FA) — an oral therapy derived from bacteria and engineered to cross a barrier protecting the brain — is now underway, having dosed its first participant. The Phase 1 study (NCT07869654), sponsored by the California-based biotech, is…
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This morning, I rolled into my office and found papers scattered across my desk. It looked as though a mischievous sprite had emptied the file cabinet. Unfortunately, I knew the sprite was me. Being organized makes life with Friedreich’s ataxia (FA) easier. When everything has an accessible home, I…
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I have a framed anonymous saying beside my bed that reads, “There are so many beautiful reasons to be happy.” I see it at least twice a day, and it makes me think about the things in my life I take for granted, dismiss as common, or that can be…
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Solid Biosciences‘ experimental gene therapy for Friedreich’s ataxia (FA), called SGT-212, has been granted orphan drug status in the European Union. This designation aims to offer additional incentives to companies investing in treatments for rare diseases, where the small number of patients can make it hard for drug…
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Becoming educated and informed about FA is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your FA journey.
There is no cure for FA yet, but here you can find more information about current therapeutic approaches, as well as experimental treatments that are in the pipeline.
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