Low-dose CTI-1601 safely increases frataxin in skin, mouth cells
CTI-1601, an experimental therapy by Larimar Therapeutics, is generally well tolerated by people with Friedreich’s ataxia (FA) and increases the levels of frataxin, a protein they’re missing, in their skin and mouth (buccal) cells after two weeks. That’s according to top-line data from the first group of patients…