How long should I wait to see the results of nomlafobusp?

Efficacy results of nomlafobusp in clinical trials are still scarce, so more data will be needed to have an indication of how soon patients may see benefits with treatment. Data from Phase 1 (NCT04519567) and Phase 2 (NCT05579691) trials suggest consistent increases in levels of frataxin, the protein whose shortage is a hallmark of Friedreich’s ataxia, about two weeks into therapy, but whether and how that will translate into clinical benefits remains to be determined.