How does nomlafobusp help with FA?
Category:
CTI-1601
Nomlafobusp is an experimental therapy that is not yet approved for the treatment of Friedreich’s ataxia. It is designed to deliver a functional version of frataxin — a protein whose shortage causes Friedreich’s ataxia — to help improve the functionality of mitochondria, the so-called “powerhouses” of cells. This is expected to help ease FA symptoms.