Friedriech’s ataxia (FA) affects growth and weight in both adult and children, with the degree of differences from the general public in these key measures of health associated with disease severity, a study based on data from a large patient group reported. While children showed a markedly higher prevalence…
Clinical trials are more attractive to people with ataxias — including those with Friedreich’s ataxia (FA) — when they target specific symptoms, such as walking and balance issues; provide potential benefits to patients and others; and cover costs of travel and accommodation, according to a recent study. These were…
A retrospective study by the National Institutes of Health (NIH) suggests that healthcare costs for those with rare diseases have been underestimated, possibly being three to five times higher than for those without rare diseases. This study provides evidence of the potential effect rare diseases may have on public health…
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