To minimize risk during the COVID-19 pandemic, Reata Pharmaceuticals is implementing at-home visits to deliver omaveloxolone to Friedreich’s ataxia (FA) patients and to assess the treatment’s safety in an extension study of the MOXIe Phase 2 clinical trial. “The COVID-19 pandemic presents an unprecedented threat to public…
Abnormally low levels of the protein HAX-1 correlate with decreased amounts of frataxin in cells from people with Friedreich’s ataxia (FA), suggesting this protein could be used as a biomarker in the disease. The study with that finding, “Frataxin deficiency in Friedreich’s ataxia is associated with reduced…
The first therapy development program for neurological disorders launched by Exicure will focus on Friedreich’s ataxia (FA), the company announced. Its FA program will be developed in collaboration with the Friedreich’s Ataxia Research Alliance (FARA), it added. FA is caused by the expansion of the GAA trinucleotide repeat in…
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