Reata Pharmaceuticals has completed a rolling submission of a new drug application (NDA) seeking approval in the U.S. for…
Articles by Steve Bryson, PhD
Reduced thickness of the peripapillary retinal nerve fiber layer (RNFL) in the eye’s retina is associated with worse disease severity…
People who have interruptions in a specific part of their GAA repeats in the FXN gene experience the onset of…
In addition to three recruiting clinical studies that were announced in June, an additional trial is seeking participants with…
Truncated forms of frataxin, the protein that is lost in people with Friedreich’s ataxia (FA), were found predominantly in…
After nearly one year of its use, omaveloxolone (RTA 408) significantly improved neurological function across several clinical…
The natural antioxidant epicatechin significantly improves heart structure and function in young people with…
Endurance exercise prevented the onset of symptoms without the need to restore frataxin production in a…
SNH6, a new dual-action therapy, has the potential to restore mitochondria function and may ultimately be used to…
Symptoms of depression significantly affect the quality of life of people with Friedreich’s ataxia (FA), a study…