The Institute for Gene Therapies (IGT) has launched, with the aim of maximizing the potential of gene therapies…
Articles by Mary Chapman
An abundance of events are afoot around the world to mark Rare Disease Day 2020 on Feb. 29. The…
Kevin Schaefer hadn’t been in an airport since he was 4 years old, so he had been looking forward to…
The Muscular Dystrophy Association (MDA) has awarded AavantiBio $1,076,232 to advance the biotechnology company’s development of a…
Online forums have markedly altered how patients, caregivers and healthcare professionals communicate and connect. Even when miles apart,…
A new data-sharing platform recently launched by the Critical Path Institute’s (C-Path) Data Collaboration Center (DCC) and the…
Scores of events are afoot worldwide to mark Feb. 28, Rare Disease Day 2019. The activities aim to raise awareness about…
Neurocrine Biosciences and Voyager Therapeutics have formed an alliance in hopes of bringing potentially life-changing treatments to market…
The U.S. Food and Drug Administration(FDA) is updating its 2015 draft guidelines for drug discovery in rare diseases, with…