Functional assessments, such as a test of how far an individual can walk in one minute, may be useful for…
Articles by Lila Levinson, PhD
People with Friedreich’s ataxia (FA) show distinct changes in the blood proteins neurofilament light chain (NfL) and tau that…
Genetic mutations causing Friedreich’s ataxia (FA) and influencing disease severity may be more complex than previously understood, according to…
An experimental therapy may help increase the protein that’s missing or deficient in Friedreich’s ataxia (FA) in people with…
The U.S. Food and Drug Administration (FDA) has granted breakthrough therapy designation to LX2006, a gene therapy for cardiomyopathy…
Biogen has initiated dosing in a Phase 3 clinical trial, called BRAVE, that’s testing the oral therapy Skyclarys…
A new gene editing technique disrupted the mutations that cause Friedreich’s ataxia (FA) in a mouse model, a study…