News

Young Rapper Hopes to Inspire Others With His New Book

Jacob Thompson began to hear an incessant ticking noise emanating from the engine of his 2002 Jeep Grand Cherokee. He played music to drown it. In doing so, he ignored a looming problem that ultimately put his car out of commission. That’s the metaphor Thompson uses when he describes his…

New Deadlines Announced for FARA Grants Program

The Friedreich’s Ataxia Research Alliance (FARA) has announced upcoming deadlines for its grants program — with awards of up to $250,000 on offer — for scientists seeking to advance research into the progressive disorder that primarily affects nerves and muscles. FARA’s research program supports basic, translational, and clinical…

Researchers Make New iPSC Models of Friedreich’s Ataxia

A team of scientists at Koc University in Turkey has created three new cell models of Friedreich’s ataxia (FA) derived from patients with repeat expansions in their FXN gene. The models “will facilitate studies to understand molecular mechanisms related to FRDA [Friedreich’s ataxia] pathology [disease processes] as well as therapeutic…

FDA Grants Fast Track Status to Oral Therapy Candidate Omaveloxolone

The U.S. Food and Drug Administration (FDA) has granted its fast track designation to Reata Pharmaceuticals’ oral candidate omaveloxolone for Friedreich’s ataxia (FA). Fast track status is designed to accelerate the development of investigational therapies that address unmet medical needs in serious or life-threatening conditions. It makes Reata eligible…

rideATAXIA Dallas Cycling Event Coming Up Nov. 6

This year’s rideATAXIA Dallas, a cycling event that raises money to support research into treatments for Friedreich’s ataxia, will take place Nov. 6. The event will feature in-person rides at UNT Discovery Park in Denton, Texas. Four route options are available: three, six, 27, and 50 miles. Registration…

Rare Disease Diversity Coalition Awards $600K to Combat Disparities

The Rare Disease Diversity Coalition (RDDC) awarded $600,000 in grants to ease the disparities faced by rare disease patients of color. These Impact Rare Disease Solution grants will go five RDDC steering committee working groups, which aim to identify problems for rare disease communities and advocate for solutions. The five…